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两独立样本率优效性检验

两样本率分别用 \(\hat{p}_1\)\(\hat{p}_2\) 表示,优效界值用 \(\delta\) 表示。

对于高优指标(\(\delta > 0\)),统计学假设如下:

\[ \begin{align} H_0 &: p_1 - p_2 \leqslant \delta \\ H_1 &: p_1 - p_2 \gt \delta \end{align} \]

对于低优指标(\(\delta < 0\)),统计学假设如下:

\[ \begin{align} H_0 &: p_1 - p_2 \geqslant \delta \\ H_1 &: p_1 - p_2 \lt \delta \end{align} \]

以下推导过程在边界条件 \(p_1 - p_2 = \delta\) 下进行。

Z-Test Pooled

假设 \(\bar{p}\) 表示合并总体率,则:

\[ \bar{p} = \frac{n_1 \hat{p}_1 + n_2 \hat{p}_2}{n_1 + n_2} \]

\(H_0\) 成立时,两样本的方差可以用 \(\bar{p}\) 来表示:

\[ \operatorname{Var}(\hat{p}_1 - \hat{p}_2) = \frac{\bar{p}(1-\bar{p})}{n_1} + \frac{\bar{p}(1-\bar{p})}{n_2} = \bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right) \]

Warning

事实上,\(H_0\) 成立时,其边界条件 \(p_1 = p_2 + \delta\),两组总体率不相等,强行将两组率进行合并是不合适的,实际应用中建议使用 Z-test Unpooled

可构建 \(z\) 统计量:

\[ z = \frac{\hat{p}_1 - \hat{p}_2 - \delta}{\sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)}} \sim N(0,1) \]

\(H_1\) 成立时,两样本率差的方差如下:

\[ \operatorname{Var}(\hat{p}_1 - \hat{p}_2) = \frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2} \]

可构建 \(z'\) 统计量:

\[ z' = \frac{\hat{p}_1 - \hat{p}_2 - \delta}{\sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)}} \sim N\left(\frac{p_1 - p_2 - \delta} {\sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)}}, \ \frac{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}} {\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)} \right) \]
\[ \begin{align} \text{Power} & = P\left(z' > z_{1-\alpha}\right) \\ & = 1 - \Phi\left(\frac{z_{1-\alpha} - \frac{p_1 - p_2 - \delta}{\sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)}}} {\sqrt{\frac{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)}}} \right) \\ & = 1 - \Phi\left(\frac{z_{1-\alpha} \sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)} - (p_1-p_2-\delta)} {\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \right) \\ \end{align} \]
\[ \begin{align} \text{Power} & = P\left(z' < z_{\alpha}\right) \\ & = \Phi\left(\frac{z_{\alpha} - \frac{p_1 - p_2 - \delta}{\sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)}}} {\sqrt{\frac{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)}}} \right) \\ & = \Phi\left(\frac{z_{\alpha} \sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)} - (p_1-p_2-\delta)} {\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \right) \end{align} \]
样本量公式推导

根据标准正态分布分位数的定义:

\[ \frac{z_{1-\alpha} \sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)} \pm (p_1-p_2-\delta)}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} = z_\beta \]

\(n_1 = kn_2\),由上式可解出

\[ n_2 = \frac{\left(z_{1-\alpha} \sqrt{\bar{p}(1-\bar{p})(1/k+1)} + z_{1-\beta} \sqrt{p_1(1-p_1)/k + p_2(1-p_2)}\right)^2}{(p_1-p_2-\delta)^2} \]
\[ n_1 = k n_2 \]

Z-Test Pooled with Continuity Correction

Z-Test Pooled 的基础上,添加校正项。

定义:

\[ c = \frac{1}{2}\left(\frac{1}{n_1}+\frac{1}{n_2}\right) \]

校正项的符号由检验方向决定,左侧检验时,校正项为 \(+c\),右侧检验时,校正项为 \(-c\)

\(H_0\) 成立时,可构建 \(z\) 统计量:

\[ z = \frac{\hat{p}_1 - \hat{p}_2 - \delta \pm c}{\sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)}} \sim N(0,1) \]

\(H_1\) 成立时,可构建 \(z'\) 统计量:

\[ z' = \frac{\hat{p}_1 - \hat{p}_2 - \delta \pm c}{\sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)}} \sim N\left(\frac{p_1 - p_2 - \delta \pm c}{\sqrt{\bar{p}(1-\bar{p})\left(\frac{1}{n_1} + \frac{1}{n_2}\right)}}, \frac{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}{\bar{p}(1-\bar{p})\left(\frac{1}{n_1} + \frac{1}{n_2}\right)} \right) \]
\[ \begin{align} \text{Power} = P\left(z' > z_{1-\alpha}\right) = 1 - \Phi\left(\frac{z_{1-\alpha} \sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)} - (p_1-p_2-\delta-c)} {\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \right) \end{align} \]
\[ \begin{align} \text{Power} = P\left(z' < z_{\alpha}\right) = \Phi\left(\frac{z_{\alpha} \sqrt{\bar{p}(1-\bar{p}) \left(\frac{1}{n_1} + \frac{1}{n_2}\right)} - (p_1-p_2-\delta+c)} {\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \right) \end{align} \]

Z-Test Unpooled

\(H_0\) 成立时,可构建 \(z\) 统计量:

\[ z = \frac{\hat{p}_1 - \hat{p}_2 - \delta}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \sim N(0,1) \]

\(H_1\) 成立时,可构建 \(z'\) 统计量:

\[ z' = \frac{\hat{p}_1 - \hat{p}_2 - \delta}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \sim N\left(\frac{p_1 - p_2 - \delta}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}}, \ 1\right) \]
\[ \text{Power} = P\left(z' > z_{1-\alpha}\right) = 1 - \Phi\left(z_{1-\alpha} - \frac{p_1-p_2-\delta}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \right) \]
\[ \text{Power} = P\left(z' < z_{\alpha}\right) = \Phi\left(z_{\alpha} - \frac{p_1-p_2-\delta}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \right) \]
样本量公式推导

根据标准正态分布分位数的定义:

\[ z_{1-\alpha} \pm \frac{(p_1 - p_2 - \delta)}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} = z_\beta \]

\(n_1 = kn_2\),由上式可解出:

\[ n_2 = \frac{\left(z_{1-\alpha} + z_{1-\beta}\right)^2 \left[ p_1(1-p_1)/k + p_2(1-p_2) \right]}{(p_1-p_2-\delta)^2} \]
\[ n_1 = k n_2 \]

Z-Test Unpooled with Continuity Correction

Z-Test Unpooled 的基础上,添加校正项。

定义:

\[ c = \frac{1}{2}\left(\frac{1}{n_1}+\frac{1}{n_2}\right) \]

校正项的符号由检验方向决定,左侧检验时,校正项为 \(+c\),右侧检验时,校正项为 \(-c\)

\(H_0\) 成立时,可构建 \(z\) 统计量:

\[ z = \frac{\hat{p}_1 - \hat{p}_2 - \delta \pm c}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \sim N(0,1) \]

\(H_1\) 成立时,可构建 \(z'\) 统计量:

\[ z' = \frac{\hat{p}_1 - \hat{p}_2 - \delta \pm c}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \sim N\left(\frac{p_1 - p_2 - \delta + c}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}}, \ 1\right) \]
\[ \text{Power} = P\left(z' > z_{1-\alpha}\right) = 1 - \Phi\left(z_{1-\alpha} - \frac{p_1-p_2-\delta-c}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \right) \]
\[ \text{Power} = P\left(z' < z_{\alpha}\right) = \Phi\left(z_{\alpha} - \frac{p_1-p_2-\delta+c}{\sqrt{\frac{p_1(1-p_1)}{n_1} + \frac{p_2(1-p_2)}{n_2}}} \right) \]