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单样本率等效性检验

\[ \begin{align} H_{01} &: p - p_0 \leqslant \delta_1 \text{ 或 } H_{02}: p - p_0 \geqslant \delta_2 \\ H_1 \ &: \delta_1 < p - p_0 < \delta_2 \end{align} \]

\(\delta_1\)\(\delta_2\) 为等效性界值,\(\delta_1 < 0\)\(\delta_2 > 0\),样本比例用 \(\hat{p}\) 表示。

\[ \operatorname{E}(\hat{p}) = p \]

以下推导过程在边界条件 \(p - p_0 = \delta_1\)\(p - p_0 = \delta_2\) 下进行。

Z-test using S(P0)

\(H_{01}\) 成立时,使用 \(p_0\) 计算样本比例 \(\hat{p}\) 的方差:

\[ \operatorname{Var}(\hat{p}) = \frac{(p_0+\delta_1)(1-p_0-\delta_1)}{n} \]

构建 \(z_1\) 统计量:

\[ z_1 = \frac{\hat{p}-p_0-\delta_1}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}} \sim N(0, 1) \]

\(H_1\) 成立时,构建 \(z'_1\) 统计量:

\[ z'_1 = \frac{\hat{p}-p_0-\delta_1}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}} \sim N\left(\frac{p-p_0-\delta_1}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}}, \frac{\sqrt{p(1-p)/n}}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}}\right) \]

\(H_{02}\) 成立时,使用 \(p_0\) 计算样本比例 \(\hat{p}\) 的方差:

\[ \operatorname{Var}(\hat{p}) = \frac{(p_0+\delta_2)(1-p_0-\delta_2)}{n} \]

构建 \(z_2\) 统计量:

\[ z_2 = \frac{\hat{p}-p_0-\delta_2}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}} \sim N(0, 1) \]

\(H_1\) 成立时,构建 \(z'_2\) 统计量:

\[ z'_2 = \frac{\hat{p}-p_0-\delta_2}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}} \sim N\left(\frac{p-p_0-\delta_2}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}}, \frac{\sqrt{p(1-p)/n}}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}}\right) \]

计算检验效能:

\[ \begin{align} \text{Power} & = \operatorname{Pr}(z'_1 > z_{1-\alpha} \ \cap \ z'_2 < -z_{1-\alpha}) \\ & = \operatorname{Pr}(z'_1 > z_{1-\alpha}) + \operatorname{Pr}(z'_2 < -z_{1-\alpha}) - \operatorname{Pr}(z'_1 > z_{1-\alpha} \ \cup \ z'_2 < -z_{1-\alpha}) \\ & = \operatorname{Pr}(z'_1 > z_{1-\alpha}) + \operatorname{Pr}(z'_2 < -z_{1-\alpha}) - 1 \\ & = 1 - \Phi\left(\frac{z_{1-\alpha} - \frac{p-p_0-\delta_1}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}}}{\frac{\sqrt{p(1-p)/n}}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}}}\right) + \Phi\left(\frac{-z_{1-\alpha} - \frac{p-p_0-\delta_2}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}}}{\frac{\sqrt{p(1-p)/n}}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}}}\right) - 1 \\ & = \begin{aligned}[t] 1 & - \Phi\left(\frac{z_{1-\alpha}\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n} - (p-p_0-\delta_1)}{\sqrt{p(1-p)/n}}\right) + \\ 1 & - \Phi\left(\frac{z_{1-\alpha}\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n} + (p-p_0-\delta_2)}{\sqrt{p(1-p)/n}}\right) - 1 \end{aligned} \\ & = \begin{aligned}[t] 1 & - \Phi\left(\frac{z_{1-\alpha}\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)} - (p-p_0-\delta_1)\sqrt{n}}{\sqrt{p(1-p)}}\right) \\ & - \Phi\left(\frac{z_{1-\alpha}\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)} + (p-p_0-\delta_2)\sqrt{n}}{\sqrt{p(1-p)}}\right) \end{aligned} \end{align} \]
\(\operatorname{Pr}(z'_1 > z_{1-\alpha} \ \cup \ z'_2 < -z_{1-\alpha}) = 1\) 的证明

略。

Z-test using S(P0) 连续性校正

Z-test using S(P0) 的基础上加入校正项 \(c_1\)\(c_2\)

\[ c_1 = \begin{cases} - \frac{1}{2n} & , \text{if } p \gt p_0 + \delta_1 \\ \frac{1}{2n} & , \text{if } p \lt p_0 + \delta_1 \\ 0 & , \text{if } \left| p - p_0 - \delta_1 \right| \lt \frac{1}{2n} \end{cases} \]
\[ c_2 = \begin{cases} - \frac{1}{2n} & , \text{if } p \gt p_0 + \delta_2 \\ \frac{1}{2n} & , \text{if } p \lt p_0 + \delta_2 \\ 0 & , \text{if } \left| p - p_0 - \delta_2 \right| \lt \frac{1}{2n} \end{cases} \]

\(H_{01}\) 成立时,构建 \(z_1\) 统计量:

\[ z_1 = \frac{\hat{p}-p_0-\delta_1+c_1}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}} \sim N(0, 1) \]

\(H_1\) 成立时,构建 \(z'_1\) 统计量:

\[ z'_1 = \frac{\hat{p}-p_0-\delta_1+c_1}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}} \sim N\left(\frac{p-p_0-\delta_1+c_1}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}}, \frac{\sqrt{p(1-p)/n}}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}}\right) \]

\(H_{02}\) 成立时,构建 \(z_2\) 统计量:

\[ z_2 = \frac{\hat{p}-p_0-\delta_2+c_2}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}} \sim N(0, 1) \]

\(H_1\) 成立时,构建 \(z'_2\) 统计量:

\[ z'_2 = \frac{\hat{p}-p_0-\delta_2+c_2}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}} \sim N\left(\frac{p-p_0-\delta_2+c_2}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}}, \frac{\sqrt{p(1-p)/n}}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}}\right) \]

计算检验效能:

\[ \begin{align} \text{Power} & = \operatorname{Pr}(z'_1 > z_{1-\alpha} \ \cap \ z'_2 < -z_{1-\alpha}) \\ & = \operatorname{Pr}(z'_1 > z_{1-\alpha}) + \operatorname{Pr}(z'_2 < -z_{1-\alpha}) - \operatorname{Pr}(z'_1 > z_{1-\alpha} \ \cup \ z'_2 < -z_{1-\alpha}) \\ & = \operatorname{Pr}(z'_1 > z_{1-\alpha}) + \operatorname{Pr}(z'_2 < -z_{1-\alpha}) - 1 \\ & = 1 - \Phi\left(\frac{z_{1-\alpha} - \frac{p-p_0-\delta_1+c_1}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}}}{\frac{\sqrt{p(1-p)/n}}{\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n}}}\right) + \Phi\left(\frac{-z_{1-\alpha} - \frac{p-p_0-\delta_2+c_2}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}}}{\frac{\sqrt{p(1-p)/n}}{\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n}}}\right) - 1 \\ & = \begin{aligned}[t] 1 & - \Phi\left(\frac{z_{1-\alpha}\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)/n} - (p-p_0-\delta_1+c_1)}{\sqrt{p(1-p)/n}}\right) + \\ 1 & - \Phi\left(\frac{z_{1-\alpha}\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)/n} + (p-p_0-\delta_2+c_2)}{\sqrt{p(1-p)/n}}\right) - 1 \end{aligned} \\ & = \begin{aligned}[t] 1 & - \Phi\left(\frac{z_{1-\alpha}\sqrt{(p_0+\delta_1)(1-p_0-\delta_1)} - (p-p_0-\delta_1+c_1)\sqrt{n}}{\sqrt{p(1-p)}}\right) \\ & - \Phi\left(\frac{z_{1-\alpha}\sqrt{(p_0+\delta_2)(1-p_0-\delta_2)} + (p-p_0-\delta_2+c_2)\sqrt{n}}{\sqrt{p(1-p)}}\right) \end{aligned} \end{align} \]

Z-test using S(Phat)

\(H_{01}\) 成立时,使用 \(p\) 计算样本比例 \(\hat{p}\) 的方差:

\[ \operatorname{Var}(\hat{p}) = \frac{p(1-p)}{n} \]

构建 \(z_1\) 统计量:

\[ z_1 = \frac{\hat{p}-p_0-\delta_1}{\sqrt{p(1-p)/n}} \sim N(0, 1) \]

\(H_1\) 成立时,构建 \(z'_1\) 统计量:

\[ z'_1 = \frac{\hat{p}-p_0-\delta_1}{\sqrt{p(1-p)/n}} \sim N\left(\frac{p-p_0-\delta_1}{\sqrt{p(1-p)/n}}, 1\right) \]

\(H_{01}\) 成立时,使用 \(p\) 计算样本比例 \(\hat{p}\) 的方差:

\[ \operatorname{Var}(\hat{p}) = \frac{p(1-p)}{n} \]

构建 \(z_2\) 统计量:

\[ z_2 = \frac{\hat{p}-p_0-\delta_2}{\sqrt{p(1-p)/n}} \sim N(0, 1) \]

\(H_1\) 成立时,构建 \(z'_2\) 统计量:

\[ z'_2 = \frac{\hat{p}-p_0-\delta_2}{\sqrt{p(1-p)/n}} \sim N\left(\frac{p-p_0-\delta_2}{\sqrt{p(1-p)/n}}, 1\right) \]

计算检验效能:

\[ \begin{align} \text{Power} & = \operatorname{Pr}(z'_1 > z_{1-\alpha} \ \cap \ z'_2 < -z_{1-\alpha}) \\ & = \operatorname{Pr}(z'_1 > z_{1-\alpha}) + \operatorname{Pr}(z'_2 < -z_{1-\alpha}) - \operatorname{Pr}(z'_1 > z_{1-\alpha} \ \cup \ z'_2 < -z_{1-\alpha}) \\ & = \operatorname{Pr}(z'_1 > z_{1-\alpha}) + \operatorname{Pr}(z'_2 < -z_{1-\alpha}) - 1 \\ & = 1 - \Phi\left(z_{1-\alpha} - \frac{p-p_0-\delta_1}{\sqrt{p(1-p)/n}}\right) + \Phi\left(-z_{1-\alpha} - \frac{p-p_0-\delta_2}{\sqrt{p(1-p)/n}}\right) - 1 \\ & = 1 - \Phi\left(z_{1-\alpha} - \frac{p-p_0-\delta_1}{\sqrt{p(1-p)/n}}\right) + 1 - \Phi\left(z_{1-\alpha} + \frac{p-p_0-\delta_2}{\sqrt{p(1-p)/n}}\right) - 1 \\ & = 1 - \Phi\left(z_{1-\alpha} - \frac{(p-p_0-\delta_1)\sqrt{n}}{\sqrt{p(1-p)}}\right) - \Phi\left(z_{1-\alpha} + \frac{(p-p_0-\delta_2)\sqrt{n}}{\sqrt{p(1-p)}}\right) \end{align} \]

Z-test using S(Phat) 连续性校正

Z-test using S(Phat) 的基础上加入校正项 \(c\)

\[ c_1 = \begin{cases} - \frac{1}{2n} & , \text{if } p \gt p_0 + \delta_1 \\ \frac{1}{2n} & , \text{if } p \lt p_0 + \delta_1 \\ 0 & , \text{if } \left| p - p_0 - \delta_1 \right| \lt \frac{1}{2n} \end{cases} \]
\[ c_2 = \begin{cases} - \frac{1}{2n} & , \text{if } p \gt p_0 + \delta_2 \\ \frac{1}{2n} & , \text{if } p \lt p_0 + \delta_2 \\ 0 & , \text{if } \left| p - p_0 - \delta_2 \right| \lt \frac{1}{2n} \end{cases} \]

\(H_{01}\) 成立时,构建 \(z_1\) 统计量:

\[ z_1 = \frac{\hat{p}-p_0-\delta_1+c_1}{\sqrt{p(1-p)/n}} \sim N(0, 1) \]

\(H_1\) 成立时,构建 \(z'_1\) 统计量:

\[ z'_1 = \frac{\hat{p}-p_0-\delta_1+c_1}{\sqrt{p(1-p)/n}} \sim N\left(\frac{p-p_0-\delta_1+c_1}{\sqrt{p(1-p)/n}}, 1\right) \]

\(H_{01}\) 成立时,构建 \(z_2\) 统计量:

\[ z_2 = \frac{\hat{p}-p_0-\delta_2+c_2}{\sqrt{p(1-p)/n}} \sim N(0, 1) \]

\(H_1\) 成立时,构建 \(z'_2\) 统计量:

\[ z'_2 = \frac{\hat{p}-p_0-\delta_2+c_2}{\sqrt{p(1-p)/n}} \sim N\left(\frac{p-p_0-\delta_2+c_2}{\sqrt{p(1-p)/n}}, 1\right) \]

计算检验效能:

\[ \begin{align} \text{Power} & = \operatorname{Pr}(z'_1 > z_{1-\alpha} \ \cap \ z'_2 < -z_{1-\alpha}) \\ & = \operatorname{Pr}(z'_1 > z_{1-\alpha}) + \operatorname{Pr}(z'_2 < -z_{1-\alpha}) - \operatorname{Pr}(z'_1 > z_{1-\alpha} \ \cup \ z'_2 < -z_{1-\alpha}) \\ & = \operatorname{Pr}(z'_1 > z_{1-\alpha}) + \operatorname{Pr}(z'_2 < -z_{1-\alpha}) - 1 \\ & = 1 - \Phi\left(z_{1-\alpha} - \frac{p-p_0-\delta_1+c_1}{\sqrt{p(1-p)/n}}\right) + \Phi\left(-z_{1-\alpha} - \frac{p-p_0-\delta_2+c_2}{\sqrt{p(1-p)/n}}\right) - 1 \\ & = 1 - \Phi\left(z_{1-\alpha} - \frac{p-p_0-\delta_1+c_1}{\sqrt{p(1-p)/n}}\right) + 1 - \Phi\left(z_{1-\alpha} + \frac{p-p_0-\delta_2+c_2}{\sqrt{p(1-p)/n}}\right) - 1 \\ & = 1 - \Phi\left(z_{1-\alpha} - \frac{(p-p_0-\delta_1+c_1)\sqrt{n}}{\sqrt{p(1-p)}}\right) - \Phi\left(z_{1-\alpha} + \frac{(p-p_0-\delta_2+c_2)\sqrt{n}}{\sqrt{p(1-p)}}\right) \end{align} \]